pAAV6.2FF

Adeno-associated Viral Vector (AAV) capsid  AAV6.2FF in AAV2Rep expression construct.

AAV6.2FF is an engineered lung tropic capsid that efficiently transduces both the murine lung and fetal human lung slices. This capsid differs from AAV6 by three amino acids—F129L, Y445F, and Y731F—which enhance its transduction and immune evasion capabilities while promoting localized gene expression in the lung following intranasal administration.

DOI: 10.1016/j.ymthe.2023.10.002

F129L, Y445F, and Y731F

MAADGYLPDWLEDNLSEGIREWWDLKPGAPKPKANQQKQDDGRGLVLPGYKYLGPFNGLDKGEPVNAADAAALEHDKAYDQQLKAG

DNPYLRYNHADAEFQERLQEDTSFGGNLGRAVFQAKKRVLEPLGLVEEGAKTAPGKKRPVEQSPQEPDSSSGIGKTGQQPAKKRLNFGQ

TGDSESVPDPQPLGEPPATPAAVGPTTMASGGGAPMADNNEGADGVGNASGNWHCDSTWLGDRVITTSTRTWALPTYNNHLYKQISS

ASTGASNDNHYFGYSTPWGYFDFNRFHCHFSPRDWQRLINNNWGFRPKRLNFKLFNIQVKEVTTNDGVTTIANNLTSTVQVFSDSEYQLP

YVLGSAHQGCLPPFPADVFMIPQYGYLTLNNGSQAVGRSSFYCLEYFPSQMLRTGNNFTFSYTFEDVPFHSSYAHSQSLDRLMNPLIDQYL

YFLNRTQNQSGSAQNKDLLFSRGSPAGMSVQPKNWLPGPCYRQQRVSKTKTDNNNSNFTWTGASKYNLNGRESIINPGTAMASHKDD

KDKFFPMSGVMIFGKESAGASNTALDNVMITDEEEIKATNPVATERFGTVAVNLQSSSTDPATGDVHVMGALPGMVWQDRDVYLQGPIW

AKIPHTDGHFHPSPLMGGFGLKHPPPQILIKNTPVPANPPAEFSATKFASFITQYSTGQVSVEIEWELQKENSKRWNPEVQYTSNYAKSANV

DFTVDNNGLYTEPRPIGTRFLTRPL*

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pAAV6.2FF

Price range: $1,500.00 through $3,000.00

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